Global Medical Director, Rare Diseases

Title:

Global Medical Director, Rare Diseases

Company:

Ipsen Biopharm Ltd

About Ipsen:

Ipsen is a mid-sized global biopharmaceutical company with a focus on transformative medicines in three therapeutic areas: Oncology, Rare Disease and Neuroscience. Supported by nearly 100 years of development experience, with global hubs in the U.S., France and the U.K, we tackle areas of high unmet medical need through research and innovation.

 Our passionate teams in more than 40 countries are focused on what matters and endeavor every day to bring medicines to patients in 88 countries. We build a workplace that champions human-centric leadership and fosters a culture of collaboration, excellence and impact. At Ipsen, every individual is empowered to be their true selves, grow and thrive alongside the company's success. Join us on our journey towards sustainable growth, creating real impact on patients and society

For more information, visit us at  and follow our latest news on LinkedIn and Instagram.

Job Description:

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Ipsen is a dynamic and growing global specialty-driven biopharmaceutical company focused on innovation and specialty care.

We aim to make a sustainable difference by significantly improving patients' health and quality of life and providing them with effective therapeutic solutions for unmet medical needs through differentiated and innovative medicines in Oncology, Neurosciences and Rare Diseases.

The patient is at the heart of everything we do, and we also care for our employees because they are the ambassadors who truly make the difference. We attract and develop bold, agile, entrepreneurial individuals who take full ownership of their decisions; leaders drawn by a purpose to make a direct impact through their work in people's lives.

We offer employees a wealth of fulfilling challenges & growth opportunities, and the chance to contribute within a fast-moving organisation, an organisation that is genuinely game-changing.

As Global Medical Director in Rare Diseases, you will lead the design and execution of the global medical strategy for highly specialized assets with significant unmet medical need. Reporting to the Medical Asset Lead, you will play a key role in shaping the clinical and scientific narrative, enabling evidence generation, and building trusted partnerships with the rare disease community. Your work will directly inform strategic decision-making and ensure patient-centric approaches across the product lifecycle.

Main Responsibilities:

Medical Strategy and Planning

• Lead the development and implementation of the Global Medical Plan for assigned rare disease assets, integrating the evidence generation plan, thought leader (TL) engagement strategy, and medical communications roadmap.

• Serve as a core member of the cross-functional asset team, aligning medical priorities with clinical development, regulatory, commercial, and market access strategies.

Evidence Generation and Scientific Leadership

• Drive the design and execution of global and international clinical studies and real-world evidence (RWE) programs, tailored to the unique challenges of rare disease populations (e.g., small sample sizes, genetic diversity, limited natural history data).

• Support affiliate-led studies by providing strategic and scientific input, reviewing protocols, and guiding execution to ensure consistency with global priorities.

Thought Leader Engagement and Community Partnership

• Develop and sustain collaborative relationships with global and local key opinion leaders, patient advocacy groups, and academic centers of excellence.

• Represent the company at international congresses, scientific symposia, advisory boards, and high-level stakeholder engagements, contributing as a respected medical voice in rare disease discourse.

Medical Education and Scientific Communication

• Create, validate, and deliver high-impact scientific and educational materials tailored to diverse audiences, including healthcare professionals, internal stakeholders, and patient communities.

Insight Generation and Strategic Input

• Capture and synthesize insights from medical field interactions, advisory boards, and external engagements to inform lifecycle management, clinical trial design, and access strategy.

Cross-Functional Collaboration and Influence

In order to be considered for this role you must have:

• Advanced clinical/scientific degree MD, PhD, or PharmD (or equivalent scientific/clinical training).

• Extensive experience in global medical affairs within the biopharmaceutical industry, including substantial involvement in late-phase development, global medical planning, and lifecycle management.

• Exceptional scientific communication communication and influencing skills.

• Solid understanding of the regulatory environment governing medical affairs activities If you feel that this could be the right next step for you, we would be delighted to engage with your application. 

• English fluency.

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We are committed to creating a workplace where everyone feels heard, valued, and supported; where we embrace "The Real Us". The value we place on different perspectives and experiences drives our commitment to inclusion and equal opportunities. When we include diverse ways of thinking, we make more thoughtful decisions and discover more innovative solutions. Together we strive to better understand the communities we serve. This means we also want to help you perform at your best when applying for a role with us. If you require any adjustments or support during the application process, please let the recruitment team know. This information will be handled with care and will not affect the outcome of your application.

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