Global Medical Affairs Director Rare Diseases

Title: Global Medical Affairs Director Rare Diseases

Lisez l'aperçu de cette opportunité pour comprendre quelles compétences, y compris les compétences non techniques pertinentes et la maîtrise des logiciels, sont requises.

Company: Ipsen Pharma (SAS)

About Ipsen

Ipsen is a mid-sized global biopharmaceutical company with a focus on transformative medicines in three therapeutic areas: Oncology, Rare Disease and Neuroscience. Supported by nearly 100 years of development experience, with global hubs in the U.S., France and the U.K, we tackle areas of high unmet medical need through research and innovation. Our passionate teams in more than 40 countries are focused on what matters and endeavor every day to bring medicines to patients in 88 countries. We build a workplace that champions human-centric leadership and foster a culture of collaboration, excellence and impact. At Ipsen, every individual is empowered to be their true selves, grow and thrive alongside the company’s success. Join us on our journey towards sustainable growth, creating real impact on patients and society For more information, visit us at and follow our latest news on LinkedIn and Instagram.

Job Description

Are you ready to lead and innovate in a dynamic, patient-focused biopharmaceutical company? Ipsen is a growing global specialty-driven biopharmaceutical company focused on innovation and specialty care. We aim to make a sustainable difference by significantly improving patients’ health and quality of life, providing effective therapeutic solutions for unmet medical needs through differentiated and innovative medicines in Oncology, Neurosciences, and Rare Diseases.

Why Ipsen

Patient-Focused: The patient is at the heart of everything we do, and improving their outcomes is the deliverable of every strategy. Employee Care: We care for our employees, who are the ambassadors making a real difference. Bold Leadership: We attract and develop bold, agile, entrepreneurial individuals who take full ownership of their decisions. Growth Opportunities: We offer a wealth of fulfilling challenges and growth opportunities in a fast-moving, game-changing organization.

About the Role

As Medical Director in Rare Diseases, you will lead the design and execution of the global medical strategy for highly specialized assets with significant unmet medical need. Reporting to the Medical Asset Lead, you will play a key role in shaping the clinical and scientific narrative, enabling evidence generation, and building trusted partnerships with the rare disease community. Your work will directly inform strategic decision-making and ensure patient-centric approaches across the product lifecycle.

Main Responsibilities

• Medical Strategy and Planning Lead the development and implementation of the Global Medical Plan for assigned rare disease assets, integrating the evidence generation plan, thought leader (TL) engagement strategy, and medical communications roadmap.
• Medical Strategy and Planning Serve as a core member of the cross-functional asset team, aligning medical priorities with clinical development, regulatory, commercial, and market access strategies.
• Medical Strategy and Planning Contribute to indication-specific medical budget planning and ensure efficient allocation of resources in line with strategic objectives.
• Evidence Generation and Scientific Leadership Drive the design and execution of global and international clinical studies and real-world evidence (RWE) programs, tailored to the unique challenges of rare disease populations.
• Evidence Generation and Scientific Leadership Support affiliate-led studies by providing strategic and scientific input, reviewing protocols, and guiding execution to ensure consistency with global priorities.
• Evidence Generation and Scientific Leadership Ensure full compliance with GCP, ethical standards, and internal medical governance; establish fit-for-purpose oversight mechanisms for all data-generating activities.
• Thought Leader Engagement and Community Partnership Develop and sustain collaborative relationships with global and local key opinion leaders, patient advocacy groups, and academic centers of excellence.
• Thought Leader Engagement and Community Partnership Represent the company at international congresses, scientific symposia, advisory boards, and high-level stakeholder engagements, contributing as a respected medical voice in rare disease discourse.
• Thought Leader Engagement and Community Partnership Partner with external stakeholders to identify opportunities for research collaborations, policy shaping, and medical education aligned with the Global Medical Affairs strategy.
• Medical Education and Scientific Communication Create, validate, and deliver high-impact scientific and educational materials tailored to diverse audiences,